Advisory Council on Rare Diseases and Personalized Medicine
Meeting information is retained on this page for 7 years then sent to the Missouri State Archives.
Register for Public Comment
Any interested party shall be granted the opportunity for clinically relevant public comment for up to five (5) minutes per medication under review by the DUR Board. The responsibility of scheduling the presentation shall rest with the interested party. Interested parties representing a manufacturer shall be granted five (5) minutes in the aggregate per medication under review by the DUR Board.
2024
October 09, 2024
- Pharmacy October 2024
- Edit Implementation Schedule through February 2025
- Sickle Cell Disease Annual Report October 2024
- Sickle Cell Disease Proposal October 2024
- Gene Therapies for Sickle Cell Disease and Beta-Thalassemia Proposal October 2024
- Bile Salt Proposal October 2024
- Iqirvo (elafibranor) NDFB October 2024
- Complement Inhibitors Systemic Proposal October 2024
- Voydeya (danicopan) NDFB October 2024
- Duchenne Muscular Dystrophy Proposal October 2024
- Elevidys (delandistrogene moxeparvovec-rokl) NDFB October 2024
- Epidermolysis Bullosa Proposal October 2024
- Filsuvez (birch triterpenes) NDFB October 2024
- Hemophilia Gene Therapy Agents Proposal October 2024
- Beqvez (fidanacogene elaparvovec-dzkt) NDFB October 2024
- Winrevair Proposal October 2024
- Winrevair (sotatercept-csrk) NDFB October 2024
- Xolremdi Proposal October 2024
- Xolremdi (mavorixafor) NDFB October 2024
July 10, 2024
April 10, 2024
- Pharmacy April 2024
- Edit Implementation Schedule through August 2024
- Adzynma Proposal April 2024
- Adzynma (ADAMTS13, recombinant-krhn) NDFB April 2024
- Pompe Disease Proposal April 2024
- Pombiliti (cipaglucosidase alfa-atga) and Opfolda (miglustat) NDFB April 2024
- Gene Therapies for Sickle Cell Disease and Beta-Thalassemia Proposal April 2024
- Therapies for Sickle Cell Disease and Beta-Thalassemia Comparison
- Casgevy (exagamglogene autotemcel) NDFB April 2024
- Lyfgenia (lovotibeglogene autotemcel) NDFB April 2024
- Zynteglo (betibeglogene autotemcel) NDFB April 2024
January 10, 2024
- Pharmacy January 2024
- Edit Implementation Schedule for April 2024
- Duchenne Muscular Dystrophy Proposal January 2024
- Hemophilia Gene Therapy Agents January 2024
- Sohonos January 2024
- C5 Compliment Inhibitors Proposal January 2024
- Elevidys (delandistrogene moxeparvovec-rokl) NDFB January 2024
- Roctavian (valoctocogene roxaparvovec-rvox) NDFB January 2024
- Sohonos (palovarotene) NDFB January 2024
- Veopoz (pozelimab-bbfg) NDFB January 2024
2023
October 11, 2023
- Edit Implementation Schedule October 2023
- Pharmacy October 2023
- Sickle Cell October 2023
- Sickle Cell Proposal October 2023
- SMA Proposal October 2023
- NMOSD Proposal October 2023
- C5 Complement Inhibitor October 2023
- Generalized Myesthenia Gravis Proposal October 2023
- Skyclarys Proposal October 2023
- Vyjuvek Proposal October 2023
- Rystiggo NDFB October 2023
- Skyclarys NDFB October 2023
- Vyjuvek NDFB October 2023
July 12, 2023
- Edit Implementation Schedule July 2023
- Givlaari Proposal July 2023
- Tzield Proposal July 2023
- Daybue Proposal July 2023
- Filspari Proposal July 2023
- Joenja Proposal July 2023
- Lamzede Proposal July 2023
- Givlaari™ NDFB July 2023
- Tzield™ NDFB July 2023
- Daybue™ NDFB July 2023
- Filspari™ NDFB July 2023
- Joenja® NDFB July 2023
- Lamzede NDFB July 2023
- Pharmacy July 2023
April 12, 2023
2022
November 08, 2022
August 09, 2022
May 10, 2022
- Edit Implementation Schedule May 2022
- Pharmacy May 2022
- Besremi Proposal May 2022
- C5 Complement Inhibitor May 2022
- Enjaymo Proposal May 2022
- Enzyme Deficiency Proposal May 2022
- TIMS Proposal May 2022
- Vyvgart Proposal May 2022
- Besremi NDFB May 2022
- Enjaymo NDFB May 2022
- Pyrukynd NDFB May 2022
- Ryplazim NDFB May 2022
- Vyvgart NDFB May 2022
February 08, 2022
2021
November 09, 2021
May 11, 2021
- CAR-T Cell Therapy Proposal May 2021
- DMD Proposal May 2021
- HoFH Agents Proposal May 2021
- Imcivree Proposal May 2021
- Nulibry Proposal May 2021
- Zokinvy Proposal May 2021
- Breyanzi NDFB May 2021
- Abecma NDFB May 2021
- Amondys NDFB May 2021
- Evkeeza NDFB May 2021
- Imcivree NDFB May 2021
- Nulibry NDFB May 2021
- Zokinvy NDFB May 2021